Intracranial delivery of CLN2 reduces brain pathology in a mouse model of classical late infantile neuronal ceroid lipofuscinosis

Marco A. Passini, James C. Dodge, Jie Bu, Wendy Yang, Qi Zhao, Dolan Sondhi, Neil R. Hackett, Stephen M. Kaminsky, Qinwen Mao, Lamya S. Shihabuddin, Seng H. Cheng, David E. Sleat, Gregory R. Stewart, Beverly L. Davidson, Peter Lobel, Ronald G. Crystal

Research output: Contribution to journalArticlepeer-review

73 Scopus citations

Fingerprint

Dive into the research topics of 'Intracranial delivery of CLN2 reduces brain pathology in a mouse model of classical late infantile neuronal ceroid lipofuscinosis'. Together they form a unique fingerprint.

Medicine & Life Sciences